Australian drugmaker CSL Ltd on Tuesday set the list price of its one-time gene therapy for hemophilia B at $3.5 million, making it the world's most expensive treatment, following its approval by the U.S. health regulator.
About one in 40,000 people is affected by the condition caused by a gene mutation that hampers the body's ability to make factor IX.
The gene therapy consists of an engineered virus carrying a gene expressed in the liver to produce clotting factor IX. "We are confident this price point will generate significant cost savings for the overall healthcare system and significantly lower the economic burden of hemophilia B," the company said.Cowen analyst Joseph Thome said in a note Hemgenix's price is higher than the brokerage's estimated $1.9 million, but its consultants have been optimistic about the therapy's uptake.
The company's unit, CSL Behring, will begin commercializing the therapy under the brand Hemgenix immediately in the United States.
South Africa Latest News, South Africa Headlines
Similar News:You can also read news stories similar to this one that we have collected from other news sources.
2023 BMW M4 CSL First Drive: Takes Your Breath AwayBMW has built a modern transcendental driver’s car with the new top-dog M4.
Read more »
Miners contribute to WA infrastructure fundThe Western Australian government is partnering with the resources sector in a A$750-million Resources Community Investment Initiative (RCII), which will facilitate investment in iconic state infrastructure projects and community and social initiatives across Western Australia. Established with founding partners Rio Tinto, BHP, Hancock Prospecting, Roy Hill, Atlas Iron, Woodside Energy, Chevron Australia and Mineral Resources, the initiative provides a state government-backed platform for direct contribution to iconic infrastructure and social projects in the Western Australian community that will make our state an even better place to live for generations.
Read more »
Isla & Co. Brings Australian-Influenced Menu to Bishop ArtsIsla & Co. is a promising new addition to the thriving Bishop Arts District restaurant scene. We stopped in for a first look at this Australian-inspired one-stop shop for brunch and dinner dishes, artisan coffee, vino and spiffy signature cocktails.
Read more »
Drest Collaborates With Australian Designers, KidSuper Teams With TommyFashion gaming app Drest partnered with Sydney’s SCCI: Sherman Centre for Culture and Ideas ahead of the Australian cultural institution launching fashion and architecture hubs at London’s Design Museum.
Read more »
A Versace Retrospective, Australian Fashion Laureates WinnersTwenty-five years after his death, Gianni Versace is the subject of an upcoming retrospective at the Groninger Museum in the Netherlands that bills itself as the largest exhibition of the Italian fashion designer’s work.
Read more »